Gene Therapy (ADA-SCID)

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Genes are what keep your DNA, which is a genetic code that controls how you look and the way your body works (“What is Gene Therapy”). Each person has two copies of each gene, one passed down from mum and the other from dad (“What Is a Gene?”). However sometimes certain genes may become mutated or there are too many or too little of that gene and that may cause disorders; ADA-SCID is an example of such a disorder. ADA, adenosine deaminase deficiency, is one of the forms of SCID, severe combined immunodeficiency, which weakens the patient’s immune system. ADA-SCID has a few forms of treatment but one of the most promising ones is gene therapy. Gene therapy is a process that can manipulate one’s genes to cure a disease. Gene therapy has both

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